Laurent Servais: Congenital muscular dystrophy phenotype with excess of neuromuscular spindles in a 5-year old girl
N. Doorenweerd: The Duchenne Brain: A matter of grey and white.
N. Wein: Using out-of-frame exon skipping to induce IRES-driven expression of an N-truncated dystrophin isoform for 5’ DMD mutations
S. Duque: Intrathecal delivery of AAV9 vectors to model and rescue a large animal model of SMA